Company Registry

Lacerta Therapeutics Inc
Profile last edited on: 8/29/2019

Gene therapy
Year Founded
First SBIR Year
Latest SBIR Award
Program Status


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Location Information

12085 Research Drive Suite 46
Alachua, FL 32615
   (352) 275-7915
Multiple Locations:   
Congressional District:   03
County:   Alachua

Public Profile

Lacerta Therapeutics, Inc. is a clinical-stage gene therapy company developing treatments for central nervous system and lysosomal storage diseases using a constellation of adeno-associated virus (AAV) vector technologies. In August 2018, Sarepta Therapeutics Inc. (NASDAQ:SRPT) - formerly dba AVI BioPharma- and itself an SBIR-involved firm until 2008 - licensed exclusive worldwide rights to Lacerta Therapeutics Inc.'s gene therapy candidate for Pompe disease - an autosomal recessive metabolic disorder which damages muscle and nerve cells. Paying an initial $30M to the smaller firm, Sarepta also has options to license two additional neuro-focused candidates from Lacerta's pipeline.

Extent of SBIR involvement

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Synopsis: Awardee Business Condition

Employee Range
Revenue Range
VC funded?
Privately Held
Stock Info
IP Holdings

Awards Distribution by Agency

Most Recent SBIR Projects

Year Phase Agency Total Amount Project Title
2020 2 NIH $2,456,333
Targeting Glioblastoma Stem-Like Cells with Custom-Designed Viral Vectors

Key People / Management

  Joseph Reddy -- President & Chief Executive Office

  Edgardo Rodriguez-Lebron -- dgardo Rodríguez-Lebrón, PhD Chief Scientific Officer

  Ken Warrington -- Founder and CTO

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